Feb 15, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
In January 2019, the CMT Research Foundation began funding a research project led by Dr. Kleopas Kleopa at the Cyprus Institute of Neurology & Genetics to study a gene therapy approach to lower levels of PMP22 protein, which is the protein coded for by the gene...
Feb 10, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
Collaboration with World-Renowned Researcher Dr. James Dahlman Aims to Identify Lipid Nanoparticles for Peripheral Nervous System Delivery Using High-Throughput Screening One of the most significant challenges in Charcot-Marie-Tooth drug development is delivering...
Nov 10, 2020 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
By: Keith N. Fargo, Ph.D., Chief Scientific Officer, CMT Research Foundation The CMT Research Foundation is currently funding a research project led by AcuraStem aimed at producing effective treatments for CMT2A. Using stem cells derived from adult patients, AcuraStem...
Nov 10, 2020 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
By: Keith N. Fargo, Ph.D., Chief Scientific Officer, CMT Research Foundation The CMT Research Foundation is currently funding a research project led by Dr. Kleopas Kleopa and his team at the Cyprus Institute of Neurology & Genetics to study a gene therapy approach...
Nov 10, 2020 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
By: Keith N. Fargo, Ph.D., Chief Scientific Officer, CMT Research Foundation The CMT Research Foundation is currently funding a research project led by DTx Pharma to design genetic therapies for Charcot-Marie-Tooth disease (CMT). By attaching the genetic sequences to...
Oct 29, 2020 | Drug Development, Gene Therapy, Life with CMT, News
Unwilling to accept the slow pace of progress in Charcot-Marie-Tooth (CMT) drug development, the CMT Research Foundation’s new video series asks and answers the most pressing questions about CMT treatments and how we can deliver them faster. In this third...