Jul 8, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, News, Research news, Small Molecule Therapies, Therapy Types
The CMT Research Foundation is partnering with the University of Illinois Chicago to test a potential therapeutic for CMT1X, the second most common form of CMT, behind only CMT1A in prevalence. CMT is one of the most common inherited neurological disorders, affecting...
Jun 27, 2021 | About CMT, CMT Research Updates, CMTRF Funded Research, Drug Development, Small Molecule Therapies, Therapy Types
The CMT Research Foundation is proud to announce our latest project, a partnership between AcuraStem, a patient-based drug discovery platform company, and Dr. Alessandra Bolino, a renowned expert in CMT and the head of the Human Inherited Neuropathies Unit at the...
Apr 19, 2021 | Drug Development, Gene Therapy, News, Research news
By: Keith Fargo, Ph.D., Chief Scientific Officer Momentum is building in the development of gene therapies for Charcot-Marie-Tooth disease. Landmark back-to-back research publications offer innovative approaches to potentially curing the two most common forms of CMT....
Mar 11, 2021 | CMT Research Updates, Gene Therapy, News, Research news
If you’ve ever been frustrated by the slow pace of research progress or questioned how a single donation makes a difference, the collaboration between the CMT Research Foundation and DTx Pharma proves that one simple action, one bold move and one donation is all...
Feb 15, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
In January 2019, the CMT Research Foundation began funding a research project led by Dr. Kleopas Kleopa at the Cyprus Institute of Neurology & Genetics to study a gene therapy approach to lower levels of PMP22 protein, which is the protein coded for by the gene...
Feb 10, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
Collaboration with World-Renowned Researcher Dr. James Dahlman Aims to Identify Lipid Nanoparticles for Peripheral Nervous System Delivery Using High-Throughput Screening One of the most significant challenges in Charcot-Marie-Tooth drug development is delivering...