Treatments in Development

There are currently no known treatments or cures for Charcot-Marie-Tooth disease, but the following can help manage symptoms:

Pain medication
Braces or splints that support the feet and ankles
Custom-made shoes or shoe inserts
Physical therapy to help the muscles remain strong and flexible
Occupational therapy to strengthen the muscles used for writing, gripping and other everyday tasks
Surgery to correct joint deformities
Hearing aids to help with hearing loss

While no treatments or cures currently exist for CMT, the science to change that does.

Now that scientists know of more than 100 gene mutations that cause CMT, they can work to develop drugs that will target those genes or their functions. The CMT Research Foundation is solely focused on funding CMT research that has the promise to deliver safe and effective treatments for people with all forms of CMT. By pursuing creative and unconventional strategies to advance scientific discovery and partnering with researchers, medical experts, industry leaders and patients, we’re speeding urgently needed progress and answers to families once and for all.

Research Approach

Research We Fund

CMT Drug Development Pipeline