The CMT Research Foundation: Delivering Treatments and Cures for Charcot-Marie-Tooth

WHO WE ARE

The CMT Research Foundation is a patient-led, non-profit focused solely on delivering treatments and cures for Charcot-Marie-Tooth disease. CMT affects one in 2,500 people (about the same prevalence as multiple sclerosis), including 150,000 Americans and more than 3 million people around the world.

The CMT Research Foundation is unlike any other CMT organization. We have one single mission: to raise funds to invest in science that will lead to treatments and cures for CMT. Our impact goes beyond simply making investments. We identify key problems or gaps in progress to a cure, then aggressively find partners to attack the problems. We introduce CMT to the greater drug development community, something that has rapidly increased the number of experts working to solve the disease.

We fund projects with the highest likelihood of leading to clinical trials and approved treatments in the near term. All investments are gated, meaning projects need to achieve milestones defined for each phase of work before receiving funding for the next. Every contract includes a return on the CMT Research Foundation’s initial investment which is then reinvested in new projects.

New Project Announcement

A partnership with Vanderbilt School of Medicine to that seeks to treat the problem of overproduction of PMP22, the primary genetic cause of CMT1A.

New Project Announcement

CMTRF and Nanite partner together to design polymer nanoparticles (PNPs), an emerging technology for drug development.

New Project Announcement

A new collaboration with Augustine Therapeutics for small molecule inhibitors of HDAC6.

Address

4062 Peachtree Road
Suite A209
Atlanta, GA 30319

Phone Number

404.806.7180

Media Inquiries

George Simpson

203.521.0352

[email protected]