Apr 19, 2021 | Drug Development, Gene Therapy, News, Research news
By: Keith Fargo, Ph.D., Chief Scientific Officer Momentum is building in the development of gene therapies for Charcot-Marie-Tooth disease. Landmark back-to-back research publications offer innovative approaches to potentially curing the two most common forms of CMT....
Mar 11, 2021 | CMT Research Updates, Gene Therapy, News, Research news
If you’ve ever been frustrated by the slow pace of research progress or questioned how a single donation makes a difference, the collaboration between the CMT Research Foundation and DTx Pharma proves that one simple action, one bold move and one donation is all...
Feb 15, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
In January 2019, the CMT Research Foundation began funding a research project led by Dr. Kleopas Kleopa at the Cyprus Institute of Neurology & Genetics to study a gene therapy approach to lower levels of PMP22 protein, which is the protein coded for by the gene...
Feb 10, 2021 | CMT Research Updates, CMTRF Funded Research, Drug Development, Gene Therapy, Research news
Collaboration with World-Renowned Researcher Dr. James Dahlman Aims to Identify Lipid Nanoparticles for Peripheral Nervous System Delivery Using High-Throughput Screening One of the most significant challenges in Charcot-Marie-Tooth drug development is delivering...
Jan 29, 2021 | Drug Development, News, Research news
What progress can patients and families expect to see in CMT research during 2021? What is the most promising research on the horizon? The CMT Research Foundation’s Chief Scientific Officer Keith Fargo, Ph.D., sat down with us to answer your most pressing questions...
Jan 11, 2021 | About CMT, CMT Research Updates, Drug Development, News, Research news
By: Susan Ruediger, CEO, CMT Research Foundation It costs more than $2.6 billion to develop an approved prescription medicine (Journal of Health Economics, 2016) and typically takes between 10 to 15 years to get a drug to clinical trials (Neuron, 2014). With no...
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