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Drug Development

Update on NMD Pharma’s Phase 2a SYNAPSE-CMT Study

Update on NMD Pharma’s Phase 2a SYNAPSE-CMT Study

Feb 3, 2026 | Drug Development

We are sharing an update from NMD Pharma regarding topline results from their Phase 2a clinical study called SYNAPSE-CMT. This clinical study explored whether the new, investigational drug ignaseclant (formerly NMD670), could provide benefit adults with...

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Applied Therapeutics to Meet With FDA on New Drug Application for the Treatment of CMT-SORD

Applied Therapeutics to Meet With FDA on New Drug Application for the Treatment of CMT-SORD

Aug 14, 2025 | CMT Research Updates, Drug Development, Research News

Applied Therapeutics, who will be speaking at the 2025 Global CMT Research Convention, recently announced that they will be meeting with the U.S. Food and Drug Administration, during the third quarter of 2025, to discuss a potential New Drug Application for...

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