CMT News & Updates
See the latest news about CMT drug development and read stories from the CMT community that highlight why we must deliver treatments and cures during our lifetime.
What Makes This CMT Research Convention Our Most Hands-On Event Yet
The Global CMT Research Convention has always been a place where patients hear directly from the scientists and companies working on their behalf. This year, on Saturday, September 26 in Cambridge, MA, Patient Day goes a step further. It's no longer just a day to...
Five Reasons to Consider a Planned Gift to CMTRF
Charcot-Marie-Tooth research is moving faster than ever, and planned gifts to the CMT Research Foundation (CMTRF) help make sure that momentum doesn't stop until there are treatments and cures for every person with CMT. A planned gift is a commitment you make today...
Project Report: A Negative Result Points to the Way Forward in CMT4B
A recent study found that a drug that helps other nerve diseases makes CMT4B1 worse, and figuring out why has opened a more promising path toward treatment, including a possible path forward for the related subtype CMT4B2. This work was funded jointly by the Muscular...
CMT Orgs Come together to Advocate for New Clinical Trial Framework
Organizations focused on Charcot-Marie-Tooth (CMT) disease have aligned with clinicians, and pharmaceutical companies to share a set of recommendations for how CMT clinical trials should be designed, with the recommendations published in Journal of the Peripheral...
The Promise Society: A New Way to Support CMT Research
There are moments when the future you've been fighting for finally comes into view. For the CMT Research Foundation, this is one of those moments. Because of our community, we are closer than ever to changing what it means to live with CMT. The research we're funding...
Deadline Extended: Submit Your Abstract for the 2026 Global CMT Research Convention
We're extending our abstract submission deadline for oral presentations. The original oral presentation abstract deadline for the 2026 Global CMT Research Convention has passed, and we want to give more researchers and clinicians the chance to share their work. The...
Apply Now: Emerging Researcher Forum at the 2026 Global CMT Research Convention
The Emerging Researcher Forum is a closed, invite-only session held the morning of Day One of the 2026 Global CMT Research Convention, ahead of the main Convention program that kicks off that afternoon. Eligible forum attendees will receive complimentary...
The Full Agenda: 2026 Global CMT Research Convention
Charcot-Marie-Tooth disease drug development is at a pivotal moment. More active drug trials are underway than ever before, and a growing community of researchers, companies, investors, and patients is working toward treatments. The Global CMT Research...
WEBINAR: Behind the Scenes, 2026 Global CMT Research Convention Preview
Charcot-Marie-Tooth disease drug development is at a pivotal moment, with more active drug trials underway than ever before and a growing community of researchers, companies, investors, and patients working toward treatments. The Global CMT Research Convention exists...
Taking Aim at CMT1J with a genetic medicine
The CMT Research Foundation, in partnership with the 1J Foundation, has funded a new study at the University of Miami led by Dr. Stephan Züchner to evaluate a newly-identified genetic variant linked to Charcot-Marie-Tooth disease type 1J and to test whether a targeted...
