CMT Endgame - Ending The Legacy of CMT1A
It’s time to put an end to CMT1A.
The suffering cannot persist any longer.
We envision the route towards clinical trials, treatments and ultimately, a cure.
Join us as we embark on this journey.
Together, let’s raise $10 million to advance treatments and find a cure for CMT1A.
The CMT Research Foundation is registered as a 501(c)(3) nonprofit organization. Contributions are tax-deductible to the extent permitted by law.
If you would like to donate to non-CMT1A, please click here.
The CMT Research Foundation has a strategy called ENDGAME. It is working. We are closer than ever to finding treatments and cures.
$10 million will fund the right research to develop treatments for CMT1A. For the first time in more than 45 years, I am encouraged that the science is at a point where treatments and cures are soon to be a reality.
We can do this together. We WILL cure CMT1A, then use the knowledge and science to cure ALL types of CMT.
Peter deSilva
Board Member & Campaign Chair
Former President – Retail of TD Ameritrade
Fellow, Harvard University Advanced Leadership Initiative
CMT1A: A Debilitating Disease with No Treatments Available, Yet.
3 Reasons Why We’re at a Critical Point:
- Gene therapies are rapidly coming online, and new genomic testing capabilities are available.
- Pharmaceutical companies are now interested and eager to develop treatments for CMT1A.
- Companies new to CMT, in partnership with the CMT Research Foundation, have real power to catalyze and accelerate progress.
Why the CMT Research Foundation: We Make Advances Happen
The CMT Research Foundation’s Scientific Advisory Board identified five key priorities to end CMT. To date, 9 projects have been funded for CMT1A, with 5* of those preparing for clinical trials.
Why We Are Taking This Approach: Two Important Success Stories
Turning $128,000 Into $1 Billion for CMT Drug Development
Novartis acquires DTx Pharma: a company that CMTRF introduced to CMT.
Why Your Support is Needed: Imagine the Possibilities
Donors are the catalysts for the early proofs of concept to get us to our ENDGAME.
- Patient funding of projects, especially those that unlock possible new solutions, is a powerful incentive for pharmaceutical industry partners with deep pockets to make additional direct investments.
- Donor dollars support CMT Research Foundation’s early funding of pre-clinical proof of concept studies that can result in new interest from new researchers.
- CMT Research Foundation shares in the profits from commercial success, then reallocates those dollars to additional projects until all forms of CMT are conquered.
Contact
For more information, or to schedule a presentation, please contact Susan or Anna.
Susan Ruediger
Co-Founder, Chief Mission Officer 678-595-2817 [email protected]
Anna Combes
VP of Philanthropy
504-669-6984
[email protected]
Address
4062 Peachtree Road
Suite A209
Atlanta, GA 30319
Phone Number
404.806.7180