Yes, CMT can affect a child’s physical development and, in many cases, may require a child to wear leg braces and restrict their physical activities.  

There are no approved disease-modifying-therapies for CMT approved by the FDA. The CMT Research Foundation is leading on various drug development efforts to change this.   

CMTRF is focused on advancing and accelerating the development of treatments and cures for CMT. The CMT Research Foundation’s impact goes beyond simply making investments, we identify key challenges that are preventing the development of treatments, then aggressively find partners to address the challenges in order to accelerate drug development and encourage more scientists to work on CMT.

Even though there are currently no approved treatments for CMT, CMTRF believes we are getting close. Here are reasons for optimism in our search for a cure:

• We understand the barriers to drug development for CMT
• We are exploring many new forms of genetic medicines
• We build upon learnings from other diseases to accelerate progress

CMTRF has funded 24 research projects to date, five of which have drug candidates that are advancing towards human clinical trials. 

Complete list here.

They can donate to CMTRF in a variety of ways, including recurring donations, annual gifts, and gifts from estates. They can also: 

• Become an ambassador to spread the word about the importance of finding a cure. 
• Create a personal fundraising page and raise money to support critical research 
• Run a charity event with proceeds going to CMTRF 
• Attend our annual Global CMT Research Convention 
• Follow us and share our messages on Facebook, LinkedIn, Instagram, and X! 

You can become a corporate sponsor of our organization and our annual Global Research Conference, fund research, or cover our operating overhead that will free more resources directly for research. Additionally, you can lend your marketing expertise to help spread awareness of our mission.  You can also encourage your employees to give by matching all employee donations to the CMT Research Foundation.