Dedicated to Research Committed to a Cure

Investing in innovative research to find treatments and cures for Charcot-Marie-Tooth disease.

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ASGCT

CMT Research Foundation Invests in XtRNA Bio to Develop Gene Therapy for CMT2D

ASGCT

Registration is Now Open for the 2025 Global CMT Research Convention — Secure Your Early Bird Tickets Today

CMT Research Foundation Invests in Asha Therapeutics to Test Novel Drug for CMT2A

CMT affects 1 in 2,500 people in the United States and more than 3 million people worldwide.

 

There is currently no cure for CMT.

WHO WE ARE

Accelerating a cure through research funding.

The CMT Research Foundation is a patient-led non-profit 100% focused on delivering treatments and cures for Charcot-Marie-Tooth, which affects 3 million people worldwide.

Since 2018, our donors and scientists have put CMT front and center in the pharmaceutical, biotech and investor communities, making a cure for all types of CMT a not-too-distant reality.

We have funded 5 therapeutics that are in preclinical or active trials

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